The goal of this Foundation is to raise awareness and funding for Sanfilippo Syndrome.

MPS LA Walk/Run Annual Event. The National MPS Society's LA Run is one of over 20 runs nationwide. Started in 2001, when there was no treatment available for ...

INHERINET (Gene Therapy of Hematopoietic Stem Cells for Inherited Diseases), an initiative founded by seven European research institutions, accumulates the ...

MPS ML Forum is dedicated to bringing families of children affected by Mucopolysaccharidoses and Mucolipidoses together

12-year-old Benjamin Siedman has been diagnosed with Sanfilippo Syndrome, a rare & fatal inherited genetic disorder. Ben and thousands of children afflicted ...